DRUG DEVELOPMENT PIPELINE

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Editas

Pre-clinical

Pre-clinical

Therapeutic Approach

Restore CFTR Function

This program is exploring ways to correct common and rare mutations in the CFTR gene using CRISPR/Cas approaches. These technologies aim to edit DNA so that the genetic defect that leads to a faulty CFTR protein is fixed. 

Status

Laboratory studies to develop and test these technologies are underway. 

Sponsor

This program is sponsored by Editas Medicine and partially funded by Cystic Fibrosis Foundation Therapeutics (CFFT). 

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